IMMUNOBIOLOGY OF ADENO-ASSOCIATED VIRUS (AAV) TRANSDUCTION IN SKELETAL MUSCLE AND LIVER

Scientific Publications

• 2001 MOLECULAR THERAPY

  A single-step affinity column for purification of serotype-5 based adeno-associated viral vectors

• 2001 PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AME

  In vivo detection of gene expression in liver by P-31 nuclear magnetic resonance spectroscopy employing creatine kinase as a marker gene

• 2001 HUMAN MOLECULAR GENETICS

  Exchange of surface proteins impacts on viral vector cellular specificity and transduction characteristics: the retina as a model

• 2005 CURRENT GENE THERAPY

  Adeno-associated viral vectors for retinal gene transfer and treatment of retinal diseases

• 2001 JOURNAL OF VIROLOGY

  Hybrid vectors based on adeno-associated virus serotypes 2 and 5 for muscle-directed gene transfer

• 2003 PROGRESS IN RETINAL AND EYE RESEARCH

  Adeno-associated viral vectors for retinal gene transfer

• 2001 GENE THERAPY

  Adenoviral vector-mediated insulin gene transfer in the mouse pancreas corrects streptozotocin-induced hyperglycemia

• 2001 GENE THERAPY

  Pharmacologically regulated gene expression in the retina following transduction with viral vectors

• 2001 HUMAN GENE THERAPY

  Isolation of highly infectious and pure adeno-associated virus type 2 vectors with a single-step gravity-flow column