GENE THERAPY FOR METACHROMATIC LEUKODYSTROPHY
- 3 Years 1999/2002
- 74.370€ Total Award
Description unavailable
Scientific Publications
- 1998 HUMAN GENE THERAPY
Transduced fibroblasts and metachromatic leukodystrophy lymphocytes transfer arylsulfatase a to myelinating glia and deficient cells in vitro
- 2005 JOURNAL OF BIOTECHNOLOGY
Expression and purification of a human, soluble Arylsulfatase A for Metachromatic Leukodystrophy enzyme replacement therapy
- 2007 JOURNAL OF THE NEUROLOGICAL SCIENCES
Metabolic correction in oligodendrocytes derived from metachromatic leukodystrophy mouse model by using encapsulated recombinant myoblasts
